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Heredodegenerative Disorders, Nervous System - 25 Studies Found
Estado | Estudiar |
Active, not recruiting |
Nombre del estudio: A Multicenter, Multinational, Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease Condición:
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Completed |
Nombre del estudio: Neuronal Ceroid Lipofuscinosis and Associated Sleep Abnormalities Condición:
Fecha: 2013-09-25 |
Completed |
Nombre del estudio: A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy of Intracerebroventricular BMN 190 in Patients With Late-Infantile Neuronal Ceroid Lipofuscinosis (CLN2) Disease Condición:
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Recruiting |
Nombre del estudio: Clinical and Neuropsychological Investigations in Batten Disease Condición: Neuronal Ceroid Lipofuscinosis Fecha: 2013-05-17 |
Terminated |
Nombre del estudio: Collection of Cerebrospinal Fluid in Healthy Children Condición:
Fecha: 2012-08-15 Intervenciones: Other: Group 1 Collecting a small amount of cerebrospinal fluid (5 mL) from healthy children, ages 2 yrs |
Recruiting |
Nombre del estudio: AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis Condición:
Fecha: 2010-12-13 Intervenciones: Biological: AAVrh.10CUCLN2 There will be 2 dose cohorts in this study. Group A consists of 2 subjects wh |
Completed |
Nombre del estudio: Cellcept for Treatment of Juvenile Neuronal Ceroid Lipofuscinosis Condición: Juvenile Neuronal Ceroid Lipofuscinosis Fecha: 2011-07-05 Intervenciones:
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Withdrawn |
Nombre del estudio: Safety and Efficacy Study of HuCNS-SC in Subjects With Neuronal Ceroid Lipofuscinosis Condición: Neuronal Ceroid Lipofuscinosis Fecha: 2010-11-05 Intervenciones: Biological: HuCNS-SC Surgery to implant human CNS stem cells |
Recruiting |
Nombre del estudio: Safety Study of a Gene Transfer Vector (Rh.10) for Children With Late Infantile Neuronal Ceroid Lipofuscinosis Condición:
Fecha: 2010-03-22 Intervenciones:
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Recruiting |
Nombre del estudio: Genotype-Phenotype Correlations of Late Infantile Neuronal Ceroid Lipofuscinosis Condición:
Fecha: 2009-12-16 |